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公开(公告)号:US20200339638A1
公开(公告)日:2020-10-29
申请号:US16856774
申请日:2020-04-23
Applicant: Sangamo Therapeutics, Inc.
Inventor: Joseph F. Nabhan , Amrutha Pattamatta , Mohammad Samie
IPC: C07K14/435 , C12N15/86 , A61P25/28 , A61P25/00
Abstract: The present disclosure provides compositions and methods for modulating transcription of mutant C9orf72 gene alleles in patients in need thereof, including patients having a C9orf72-related disease such as amyotrophic lateral sclerosis (ALS) or frontotemporal dementia (FTD).
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公开(公告)号:US12139517B2
公开(公告)日:2024-11-12
申请号:US16856774
申请日:2020-04-23
Applicant: Sangamo Therapeutics, Inc.
Inventor: Joseph F. Nabhan , Amrutha Pattamatta , Mohammad Samie
Abstract: The present disclosure provides compositions and methods for modulating transcription of mutant C9orf72 gene alleles in patients in need thereof, including patients having a C9orf72-related disease such as amyotrophic lateral sclerosis (ALS) or frontotemporal dementia (FTD).
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公开(公告)号:US20250066434A1
公开(公告)日:2025-02-27
申请号:US18943130
申请日:2024-11-11
Applicant: Sangamo Therapeutics, Inc.
Inventor: Joseph F. Nabhan , Amrutha Pattamatta , Mohammad Samie
Abstract: The present disclosure provides compositions and methods for modulating transcription of mutant C9orf72 gene alleles in patients in need thereof, including patients having a C9orf72-related disease such as amyotrophic lateral sclerosis (ALS) or frontotemporal dementia (FTD).
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公开(公告)号:US20250066433A1
公开(公告)日:2025-02-27
申请号:US18942681
申请日:2024-11-09
Applicant: Sangamo Therapeutics, Inc.
Inventor: Joseph F. Nabhan , Amrutha Pattamatta , Mohammad Samie
Abstract: The present disclosure provides compositions and methods for modulating transcription of mutant C9orf72 gene alleles in patients in need thereof, including patients having a C9orf72-related disease such as amyotrophic lateral sclerosis (ALS) or frontotemporal dementia (FTD).
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